ASH 2023: MRD Highlights in BioPharma Drug Development

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Latest Publications

Isatuximab, carfilzomib, lenalidomide, and dexamethasone in patients with newly diagnosed, transplantation-eligible multiple myeloma (SKylaRk): a single-arm, phase 2 trial

Lancet Haematology
April 2024
Authors and Affiliates
Elizabeth O’Donnell, Clifton Mo, Andrew J Yee, Omar Nadeem, Jacob Laubach, Jacalyn Rosenblatt, Nikhil Munshi, Shonali Midha, Diana Cirstea, Pavlina Chrysafi, Nora Horick, Paul G Richardson, Noopur Raje Massachusetts General Hospital Cancer Center, Boston, MA, USA (E O’Donnell MD, A J Yee MD, D Cirstea MD, N Horick MS, Prof N Raje MD); Dana-Farber Cancer Institute, Boston, MA, USA (E O’Donnell, C Mo MD, O Nadeem MD, J Laubach MD, Prof N Munshi MD, S Midha MD, Prof P G Richardson MD); Beth Israel Deaconess Medical Center, Boston, MA, USA (J Rosenblatt MD); Mount Auburn Hospital, Cambridge, MA, USA (P Chrysafi MD); Harvard Medical School, Boston, MA, USA (E O’Donnell, C Mo, A J Yee, O Nadeem, J Laubach, J Rosenblatt, N Munshi, Prof S Midha, D Cirstea, P G Richardson, Prof N Raje)

Long-term follow-up of patients with follicular lymphoma using next generation sequencing to detect minimal residual disease

Clinical Lymphoma Myeloma & Leukemia
April 2024
Authors and Affiliates
Ayushi Chauhan2, Catherine Lai4 Frank Kuhr3, Heidi Simmons3, Bruce D. Cheson1 1- Center for Cancer and Blood Disorders, Bethesda, MD; 2- Medical College of Georgia, Augusta, Georgia; 3-Adaptive Biotechnologies, Seattle, WA; 4-University of Pennsylvania, Perelman Center for Advanced Medicine, Philadelphia, PA

Identifying immune signatures of common exposures through co-occurrence of T-cell receptors in tens of thousands of donors

May DH, et al.
bioRxiv
March 2024
Authors and Affiliates
Damon H. May 1, Steven Woodhouse 1, H. Jabran Zahid 2, Rebecca Elyanow 1, Kathryn Doroschak 1, Matthew T. Noakes 1, Ruth Taniguchi 1, Zheng Yang 1, John R. Grino 1, Rachel Byron 1, Jamie Oaks 1, Anna Sherwood 1, Julia Greissl 2, Haiyin Chen-Harris 1, Bryan Howie 1, Harlan S. Robins 1 1: Adaptive Biotechnologies - 1165 Eastlake Ave E, Seattle, WA 98109 2: Microsoft Research - 14820 NE 36th St, Redmond, WA 98052

CD22 CAR T cells demonstrate high response rates and safety in pediatric and adult B-ALL: Phase 1b results

Leukemia
March 2024
Authors and Affiliates
Liora M. Schultz1,2,6, Nikeshan Jeyakumar3,6, Anne Marijn Kramer 2, Bita Sahaf2, Hrishi Srinagesh3, Parveen Shiraz4, Neha Agarwal4, Mark Hamilton3, Courtney Erickson1, Ashley Jacobs1, Jennifer Moon1, Christina Baggott1, Sally Arai4, Sushma Bharadwaj4, Laura J. Johnston4, Michaela Liedtke3, Robert Lowsky4, Everett Meyer4, Robert Negrin4, Andrew Rezvani4, Judy Shizuru 4, Surbhi Sidana 4, Emily Egeler2, Sharon Mavroukakis2, Ramya Tunuguntla5, Nikolaos Gkitsas-Long5, Aidan Retherford5, Annie Kathleen Brown5, Anne-Louise Gramstrap-Petersen5, Raquel Martin Ibañez5, Steven A. Feldman2,5, David B. Miklos 2,4, Crystal L. Mackall 1,2, Kara L. Davis1,2, Matthew Frank2,4, Sneha Ramakrishna1,2 and Lori Muffly 2,4 1Division of Pediatric Hematology/Oncology, Stanford University, Stanford, CA, USA. 2Center for Cancer Cell Therapy, Stanford University, Stanford, CA, USA. 3Division of Hematology, Stanford University, Stanford, CA, USA. 4Division of Blood and Marrow Transplantation and Cellular Therapy, Stanford University, Stanford, CA, USA. 5Laboratory for Cell and Gene Medicine, Stanford University, Stanford, CA, USA. 6These authors contributed equally: Liora M. Schultz, Nikeshan Jeyakumar. ✉email: lmuffly@stanford.edu

Complete loss of TP53 and RB1 is associated with complex genome and low immune infiltrate in pleomorphic rhabdomyosarcoma

Beird H et al.
HGG Advances
February 2024
Authors and Affiliates
Hannah C. Beird; Chia-Chin Wu; Michael Nakazawa; Davis Ingram; Joseph R. Daniele; Rossana Lazcano; Latasha Little; Christopher Davies; Najat C. Daw; Khalida Wani; Wei-Lien Wang; Xingzhi Song; Curtis Gumbs; Jianhua Zhang; Brian Rubin; Anthony Conley; Adrienne M. Flanagan; Alexander J. Lazar and P. Andrew Futreal.

Antigen-presenting B cells promote TCF-1+ PD1-stem-like CD8+ T-cell proliferation in glioblastoma

Hou D et al.
Frontiers in Immunology
February 2024
Authors and Affiliates
David Hou; Hanxiao Wan; Joshua L. Katz; Si Wang; Brandyn A. Castro; Gustavo I. Vazquez-Cervantes; Victor A. Arrieta; Silpol Dhiantravan; Hinda Najem; Aida Rashidi; Tzu-yi Chia; Tarlan Arjmandi; Jimena Collado; Leah Billingham; Aurora Lopez-Rosas; Yu Han; Adam M. Sonabend; Amy B. Heimberger; Peng Zhang; Jason Miska and Catalina Lee-Chang.

Single-cell analysis of immune recognition in chronic myeloid leukemia patients following tyrosine kinase inhibitor discontinuation

Huuhtanen, J et al.
Nature
February 2024
Authors and Affiliates
Jani Huuhtanen; Shady Adnan-Awad; Jason Theodoropoulos; Sofia Forstén; Rebecca Warfvinge; Olli Dufva; Jonas Bouhlal; Parashar Dhapola; Hanna Duàn; Essi Laajala; Tiina Kasanen; Jay Klievink; Mette Ilander; Taina Jaatinen; Ulla Olsson-Strömberg; Henrik Hjorth-Hansen; Andreas Burchert; Göran Karlsson; Anna Kreutzman; Harri Lähdesmäki and Satu Mustjoki.
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